Safety and efficacy of intra-erythrocyte dexamethasone sodium phosphate in children with ataxia telangiectasia (ATTeST): a multicentre, randomised, double-blind, placebo-controlled phase 3 trial.

Journal: The Lancet. Neurology

Publication Year: 2024

Authors & Co-authors:  Zielen Stefan S Crawford Thomas T Benatti Luca L Magnani Mauro M Kieslich Matthias M Ryan Monique M Meyts Isabelle I Gulati Sheffali S Borgohain Rupam R Yadav Ravi R